Treatment type

Enzyme Replacement

Treatments and trials using Enzyme Replacement, with the same country and access zoom as New Developments.

Enzyme Replacement breakthroughs

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Health Canada/FDA ApprovedUnited States Canada

New Weekly Enzyme Treatment for Arginase-1 Deficiency

Loargys (pegzilarginase-nbln) for arginase-1 deficiency (ARG1-D)

The FDA (accelerated, 23 Feb 2026) and Health Canada (full NOC, 29 May 2026) have labelled a weekly enzyme replacement for hyperargininemia in people 2 years…

The FDA (accelerated, 23 Feb 2026) and Health Canada (full NOC, 29 May 2026) have labelled a weekly enzyme…

September 7, 2026