Condition

Leukocyte Adhesion Deficiency Type I

Treatments and trials tagged Leukocyte Adhesion Deficiency Type I, with the same country and access zoom as New Developments.

All New Developments

Leukocyte Adhesion Deficiency Type I breakthroughs

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FDA ApprovedUnited States

First FDA-Approved Gene Therapy for Severe Leukocyte Adhesion Deficiency

KRESLADI (marnetegragene autotemcel) — one-time gene therapy for children with severe leukocyte adhesion deficiency type I when no matched sibling donor is available

FDA accelerated approval on 26 March 2026 for KRESLADI (marnetegragene autotemcel) suspension — an autologous hematopoietic stem cell-based gene…

This is for families of children with severe LAD-I from confirmed ITGB2 gene changes who do not have an…