Condition

Cerebral Adrenoleukodystrophy

Treatments and trials tagged Cerebral Adrenoleukodystrophy. Filter by country, access level, or patient stories.

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EMA AuthorisedEuropean Union

First EU Medicine for Early Brain ALD in Boys Ages 2–12

Nezglyal (leriglitazone) — oral suspension for early cerebral adrenoleukodystrophy (Gd-negative)

The European Commission authorised Nezglyal (leriglitazone) on 21 September 2026, under exceptional circumstances.

This is for boys aged 2 to 12 with early cerebral adrenoleukodystrophy (cALD) — Gd-negative brain lesions on MRI and a Neurological Functional Score of 0 or 1…

September 25, 2026