New Weekly Enzyme Treatment for Arginase-1 Deficiency
Loargys (pegzilarginase-nbln) for arginase-1 deficiency (ARG1-D)
The FDA (accelerated, 23 Feb 2026) and Health Canada (full NOC, 29 May 2026) have labelled a weekly enzyme replacement for hyperargininemia in people 2 years…
Loargys (pegzilarginase) is a weekly enzyme treatment for arginase 1 deficiency in people 2 and older, used with a low-protein diet.