Condition

Arginase-1 Deficiency

Treatments and trials tagged Arginase-1 Deficiency, with the same country and access zoom as New Developments.

All New Developments

Arginase-1 Deficiency breakthroughs

All countriesUnited StatesCanadaUnited KingdomJapanChinaAustraliaSwitzerlandEuropean UnionNewestPatient Stories
Health Canada/FDA ApprovedUnited StatesCanada

New Weekly Enzyme Treatment for Arginase-1 Deficiency

Loargys (pegzilarginase-nbln) for arginase-1 deficiency (ARG1-D)

The FDA (accelerated, 23 Feb 2026) and Health Canada (full NOC, 29 May 2026) have labelled a weekly enzyme replacement for hyperargininemia in people 2 years…

The FDA (accelerated, 23 Feb 2026) and Health Canada (full NOC, 29 May 2026) have labelled a weekly enzyme…