FDA ApprovedUnited States
First FDA-Approved Treatment for Alexander Disease
Zanvastro (zilganersen) for Alexander disease (AxD)
The first FDA-labelled medicine for Alexander disease — an ultra-rare, progressive GFAP leukodystrophy. On 3 September 2026 the FDA approved Zanvastro…
The first FDA-labelled medicine for Alexander disease — an ultra-rare, progressive GFAP leukodystrophy. On…