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Compassionate AccessUnited StatesEuropean Union

First EU-Authorised Treatment for MCT8 Deficiency (Allan-Herndon-Dudley)

Emcitate (tiratricol) — dispersible tablets for peripheral thyrotoxicosis in MCT8 deficiency

European Commission marketing authorisation 12 February 2025 for Emcitate (tiratricol) 350 microgram dispersible tablets — treatment of…

This is for people living with MCT8 deficiency (Allan-Herndon-Dudley syndrome) — and the caregivers who help…