New Weekly Enzyme Treatment for Arginase-1 Deficiency

Who this is for

Next clinical step

Health Canada and the US Food and Drug Administration (FDA) have approved this medicine. In Canada and the United States, ask your doctor or a specialist whether it suits you. They can write a prescription. Insurance or public drug plan coverage is not guaranteed. In Canada, it is authorised but may not be on sale yet.

Ways to access this treatment

• United States · Prescription

  US prescription (FDA-labelled)

  https://dailymed.nlm.nih.gov/dailymed/lookup.cfm?setid=d5ceabf2-43a0-4746-9371-d98a39cf6cfc

Possible routes (not confirmed)

• Canada · Prescription · Applicability unknown

  Canada prescription (Health Canada NOC, DIN 02568713)

  Health Canada issued a Notice of Compliance (NOC) on 2026-05-29 (DIN 02568713), but the Drug Product Database does not list it as marketed yet; Canadian supply date not confirmed.

  https://health-products.canada.ca/api/drug/drugproduct/?din=02568713

General resources for further research

• Canadian Clinical Trial Search Portal (Health Canada)

  Health Canada's public search of the drug and biologic clinical trials it has authorised in Canada (phase 1 to 3, since April 2013). Search by condition, drug, or trial status and see where trials are running. It replaced the Health Canada Clinical Trials Database in July 2026. A listing is not enrolment, and Health Canada does not recruit patients: ask your clinician and contact the trial sponsor.

  https://clinical-trials-search.canada.ca/en/home

• ClinicalTrials.gov

  US National Library of Medicine registry of clinical studies. Search by condition, drug, NCT number, and location. A listing is not enrolment, eligibility, or funding. Talk with the trial contact and a clinician before assuming a slot exists.

  https://clinicaltrials.gov/